Rare Disease companies

ANI Pharmaceuticals is a Nasdaq-listed biopharmaceutical company developing, manufacturing, and marketing branded and generic prescription drugs, with U.S. manu…

Alexion Pharmaceuticals develops and delivers transformative medicines for rare diseases, specialising in complement system biology treatments.

Baylor Genetics is a diagnostic genomics company offering genetic testing services - including WGS, WES, and RNA Sequencing - across rare diseases, pediatrics,…